Category: News
Launch of Critical Path to Therapeutics for the Ataxias (CPTA) Consortium
SCA & ARCA Global Conference 2020 – recorded sessions/flash talks & abstracts
SARA training tool by DZNE
Research article: “Toward allele-specific targeting therapy and pharmacodynamic marker for spinocerebellar ataxia type 3”
European Spinocerebellar Ataxia Type 3/Machado-Joseph Disease Initiative (ESMI) –lay summary of the results of this 4-year Consortium study
Research article: “Conversion of individuals at risk for spinocerebellar ataxia types 1, 2, 3, and 6 to manifest ataxia (RISCA): a longitudinal cohort study”
SCA & ARCA Global Conference 2020 moves online!
ARCA Global Conference POSTPONED
Report – First SCA Global Conference
Conference information
The first conference of the SCA Global initiative was held in Las Vegas from 27 to 29 March 2019. Researchers from around the world, industry and patient organizations have formed a global collaboration in clinical research efforts for Spinocerebellar Ataxias (SCA). SCA Global was created to address the obstacles that clinical investigators are having with a lack of natural history study data and validated biomarkers for Ataxia.
Conference programme
Please find here the programme of the 1st SCA Global Conference.
Conference Sponsors
In view of the emerging treatment for SCAs, there is the urgent need to increase trial readiness. To this end, SCA Global will strive to achieve the following objectives:
- to provide added value through a global SCA research platform that is based on exchange and sharing
- to establish large, well characterized, standardised trial ready cohorts,
- to precisely define the evolution of clinical outcomes across all SCAs and different world regions,
- to better characterise the pre-ataxia stage of all SCAs,
- to develop and validate imaging and biochemical biomarkers,
- to attract young talent and to improve education and training of clinical investigators.
Outcome of the conference
As an outcome of the SCA Global conference four working groups (WGs) were formed:
- Clinical outcome assessments (COAs)
- MR biomarkers
- Standards of biosampling
- SCA Global policies
ERN-RND will be partnering with SCA Global. Two of the four working groups will be led by ERN-RND members: Thomas Klockgether leads the Clinical Outcome Assessment WG and Holm Graessner leads the SCA Global Policies WG.
SCA Global Conference 2020
The next SCA Global conference will be organised in April 2020 in Bonn, Germany.