Viewpoint: “Paving the Way Toward Meaningful Trials in Ataxias: An Ataxia Global Initiative Perspective” Continue reading “Viewpoint: “Paving the Way Toward Meaningful Trials in Ataxias: An Ataxia Global Initiative Perspective””
Review article: “The ARCA Registry: A Collaborative Global Platform for Advancing Trial Readiness in Autosomal Recessive Cerebellar Ataxias” Continue reading “Review article: “The ARCA Registry: A Collaborative Global Platform for Advancing Trial Readiness in Autosomal Recessive Cerebellar Ataxias””
Launch of Critical Path to Therapeutics for the Ataxias (CPTA) Consortium Continue reading “Launch of Critical Path to Therapeutics for the Ataxias (CPTA) Consortium”
SCA & ARCA Global Conference 2020 – recorded sessions/flash talks & abstracts Continue reading “SCA & ARCA Global Conference 2020 – recorded sessions/flash talks & abstracts”
Research article: “Toward allele-specific targeting therapy and pharmacodynamic marker for spinocerebellar ataxia type 3” Continue reading “Research article: “Toward allele-specific targeting therapy and pharmacodynamic marker for spinocerebellar ataxia type 3””
European Spinocerebellar Ataxia Type 3/Machado-Joseph Disease Initiative (ESMI) –lay summary of the results of this 4-year Consortium study Continue reading “European Spinocerebellar Ataxia Type 3/Machado-Joseph Disease Initiative (ESMI) –lay summary of the results of this 4-year Consortium study”
Research article: “Conversion of individuals at risk for spinocerebellar ataxia types 1, 2, 3, and 6 to manifest ataxia (RISCA): a longitudinal cohort study” Continue reading “Research article: “Conversion of individuals at risk for spinocerebellar ataxia types 1, 2, 3, and 6 to manifest ataxia (RISCA): a longitudinal cohort study””
SCA & ARCA Global Conference 2020 moves online! Continue reading “SCA & ARCA Global Conference 2020 moves online!”