Brief report: “Polyglutamine-Expanded Ataxin-3: A Target Engagement Marker for Spinocerebellar Ataxia Type 3 in Peripheral Blood”

Brief report:Polyglutamine-Expanded Ataxin-3: A Target Engagement Marker for Spinocerebellar Ataxia Type 3 in Peripheral Blood

Authors: Jeannette Hübener-Schmid, Kirsten Kuhlbrodt, Julien Peladan, Jennifer Faber, Magda M. Santana, Holger Hengel, Heike Jacobi, Kathrin Reetz, Hector Garcia-Moreno, Mafalda Raposo, Judith van Gaalen, Jon Infante, Katharina M. Steiner, Jeroen de Vries, Marcel M. Verbeek, Paola Giunti, Luis Pereira de Almeida, Manuela Lima, Bart van de Warrenburg, Ludger Schöls, Thomas Klockgether, Matthis Synofzik, European Spinocerebellar Ataxia Type-3/Machado–Joseph Disease Initiative (ESMI) Study Group, Olaf Riess

Published: Movement Disorders, August 2021